Biography

For the past five years, I have been developing therapeutic splice-manipulating antisense oligonucleotides (AOs) mostly for rare inherited diseases. There are many rare diseases with no therapy or effective treatment strategy, compounding this is the limited funding source for this particular research area. Due to extremely low numbers of patients and often a lack of complete understanding of many diseases, the pharmaceutical industry interest in pursuing therapeutics for extremely rare diseases is very low. I would like to contribute my knowledge in therapeutic AO design to as many rare diseases as possible where there are no therapeutic options.

I am also actively promoting sciences through community engagements.

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